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Autosomal dominant medullary cystic kidney disease with or without hyperuricemia

MedGen UID:
1377523
Concept ID:
C4511620
Disease or Syndrome
Synonyms: ADTKD; autosomal dominant interstitial kidney disease; Autosomal dominant medullary cystic kidney disease; autosomal dominant medullary cystic kidney disease; autosomal dominant medullary cystic kidney disease with or without hyperuricemia; Autosomal dominant tubulointerstitial kidney disease; autosomal dominant tubulointerstitial kidney disease; Familial juvenile hyperuricemic nephropathy; MCKD; medullary cystic disease; medullary cystic kidney disease; Medullary cystic kidney disease; polycystic kidneys, medullary type
SNOMED CT: Autosomal dominant medullary cystic kidney disease (726018006); Autosomal dominant tubulointerstitial kidney disease (726018006)
Modes of inheritance:
Autosomal dominant inheritance
MedGen UID:
141047
Concept ID:
C0443147
Intellectual Product
Source: Orphanet
A mode of inheritance that is observed for traits related to a gene encoded on one of the autosomes (i.e., the human chromosomes 1-22) in which a trait manifests in heterozygotes. In the context of medical genetics, an autosomal dominant disorder is caused when a single copy of the mutant allele is present. Males and females are affected equally, and can both transmit the disorder with a risk of 50% for each child of inheriting the mutant allele.
 
Monarch Initiative: MONDO:0008264
Orphanet: ORPHA34149

Definition

Autosomal dominant medullary cystic kidney disease is a chronic tubulointerstitial nephropathy, which belongs to a heterogeneous group of inherited tubulo-interstitial nephritis. Less than 60 families affected have been described. Clinical onset and course are insidious. Symptoms typically appear at an average age of 28 years, when the urinary concentrating ability is markedly reduced, producing polyuria and stable low urinary osmolality in the first morning urine and lack of any compensatory effect after endonasal desmopressin. End-stage renal disease typically occurs in the third-fifth decade of life or even later. Two genes have been linked to the disease: MCKD1 (1q21) and MCKD2 (in 16p12, where the gene UMOD, encoding uromodulin or Tamm-Horsfall protein, has been identified as responsible of the disease). [from SNOMEDCT_US]

Term Hierarchy

CClinical test,  RResearch test,  OOMIM,  GGeneReviews,  VClinVar  
  • CROGVAutosomal dominant medullary cystic kidney disease with or without hyperuricemia

Professional guidelines

PubMed

Ashiq K, Bajwa MA, Tanveer S, Qayyum M, Ashiq S, Khokhar R, Abid F
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Etiology

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Diagnosis

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Prognosis

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