Disease-Associated Short Tandem Repeats Co-localize with Chromatin Domain Boundaries

Cell. 2018 Sep 20;175(1):224-238.e15. doi: 10.1016/j.cell.2018.08.005. Epub 2018 Aug 30.

Abstract

More than 25 inherited human disorders are caused by the unstable expansion of repetitive DNA sequences termed short tandem repeats (STRs). A fundamental unresolved question is why some STRs are susceptible to pathologic expansion, whereas thousands of repeat tracts across the human genome are relatively stable. Here, we discover that nearly all disease-associated STRs (daSTRs) are located at boundaries demarcating 3D chromatin domains. We identify a subset of boundaries with markedly higher CpG island density compared to the rest of the genome. daSTRs specifically localize to ultra-high-density CpG island boundaries, suggesting they might be hotspots for epigenetic misregulation or topological disruption linked to STR expansion. Fragile X syndrome patients exhibit severe boundary disruption in a manner that correlates with local loss of CTCF occupancy and the degree of FMR1 silencing. Our data uncover higher-order chromatin architecture as a new dimension in understanding repeat expansion disorders.

Keywords: 3D genome folding; TADs; fragile X syndrome; genome instability; higher-order chromatin architecture; short tandem repeats; subTADs; topologically associating domains; trinucleotide repeat expansion disorders.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, Non-P.H.S.

MeSH terms

  • Adult
  • Brain / cytology
  • Brain / pathology
  • CCCTC-Binding Factor / genetics
  • CCCTC-Binding Factor / physiology
  • Cell Line
  • Chromatin / genetics*
  • Chromatin / physiology
  • Chromatin Assembly and Disassembly / genetics
  • Chromatin Assembly and Disassembly / physiology
  • CpG Islands / genetics
  • CpG Islands / physiology
  • DNA / genetics
  • Disease / etiology
  • Disease / genetics
  • Female
  • Fragile X Mental Retardation Protein / genetics
  • Fragile X Mental Retardation Protein / metabolism
  • Fragile X Mental Retardation Protein / physiology
  • Fragile X Syndrome / genetics
  • Fragile X Syndrome / metabolism
  • Genome, Human / genetics
  • Humans
  • Male
  • Microsatellite Repeats / genetics
  • Microsatellite Repeats / physiology*
  • Trinucleotide Repeat Expansion / genetics
  • Trinucleotide Repeat Expansion / physiology*

Substances

  • CCCTC-Binding Factor
  • CTCF protein, human
  • Chromatin
  • FMR1 protein, human
  • Fragile X Mental Retardation Protein
  • DNA