DYS-HAC-iPS cells: the combination of gene and cell therapy to treat duchenne muscular dystrophy

Mol Ther. 2010 Feb;18(2):238-40. doi: 10.1038/mt.2009.303.

Author

Affiliation

¹ Department of Genetics, Yale School of Medicine, Yale Stem Cell Center, New Haven, Connecticut, USA.

No abstract available

Publication types

Comment

MeSH terms

Cell- and Tissue-Based Therapy / methods*
Chromosomes, Artificial, Human / genetics*
Dystrophin / genetics
Dystrophin / physiology*
Genetic Therapy / methods*
Humans
Induced Pluripotent Stem Cells / cytology
Induced Pluripotent Stem Cells / physiology*
Models, Theoretical
Muscular Dystrophy, Duchenne / therapy*

Substances

Dystrophin