Limitations of extensive TPMT genotyping in the management of azathioprine-induced myelosuppression in IBD patients

Clin Biochem. 2011 Sep;44(13):1062-1066. doi: 10.1016/j.clinbiochem.2011.06.079. Epub 2011 Jun 24.

Abstract

Background and aims: TPMT deficiency is associated with azathioprine (AZA)-induced myelosuppression (MS). However, in one previous study, only about ¼ of MS episodes in Crohn's Disease patients under AZA can be attributed to TPMT deficiency. Recently, new TPMT mutations have been described and our aim is to investigate their clinical relevance before and after a first MS episode on thiopurine therapy.

Methods: Clinical data from 61 IBD patients having developed MS during AZA therapy were collected. Sequencing analysis was carried out on TPMT cDNA for the presence of all currently known mutations.

Results: Only TPMT *2, *3A and *3C mutations were found in this cohort. TPMT mutations were observed in 15 out of 61 patients (25%). Four out of 15 were homozygous for a TPMT mutation (low methylator, LM genotype) and 11 were heterozygous (intermediate methylator, IM genotype). Median delays of MS onset were 2, 2.75 and 6months in the LM, IM and HM (high methylator, wild type TPMT) groups, respectively. After the first MS episode, 36 patients resumed thiopurine treatment of which 13 experienced a second MS episode. This second episode was also rarely associated with TPMT mutations.

Conclusions: One quarter of MS episodes during AZA were associated with TPMT deficient genotype. After a first leucopenia episode, thiopurine therapy may be resumed in a majority of patients independently of their TPMT genotype.

MeSH terms

  • Adolescent
  • Adult
  • Aged
  • Azathioprine / adverse effects*
  • Azathioprine / therapeutic use
  • DNA Mutational Analysis
  • Drug Hypersensitivity / complications*
  • Drug Hypersensitivity / etiology
  • Drug Hypersensitivity / genetics
  • Female
  • Genotype
  • Humans
  • Immunosuppressive Agents
  • Inflammatory Bowel Diseases / complications*
  • Inflammatory Bowel Diseases / drug therapy
  • Leukopenia
  • Male
  • Methyltransferases / genetics*
  • Middle Aged
  • Mutation
  • Pancytopenia / chemically induced
  • Pancytopenia / genetics
  • Purine-Pyrimidine Metabolism, Inborn Errors / complications*
  • Purine-Pyrimidine Metabolism, Inborn Errors / etiology
  • Purine-Pyrimidine Metabolism, Inborn Errors / genetics
  • Retrospective Studies
  • Young Adult

Substances

  • Immunosuppressive Agents
  • Methyltransferases
  • thiopurine methyltransferase
  • Azathioprine

Supplementary concepts

  • Thiopurine S methyltranferase deficiency