The risks of therapeutic misconception and individual patient (n=1) "trials" in rare diseases such as Duchenne dystrophy
Neuromuscul Disord
.
2011 Jan;21(1):13-5.
doi: 10.1016/j.nmd.2010.09.012.
Epub 2010 Nov 3.
Author
Annemieke Aartsma-Rus
1
Affiliation
1
Department of Human Genetics, Leiden University Medical Center, P.O. Box 9600, 2300 RC Leiden, The Netherlands. a.m.rus@lumc.nl
PMID:
21051233
DOI:
10.1016/j.nmd.2010.09.012
No abstract available
MeSH terms
Clinical Trials as Topic
Humans
Muscular Dystrophy, Duchenne / therapy*
Precision Medicine / methods*
Therapeutic Misconception*