Rapid immune reconstitution after a reduced-intensity conditioning regimen and a CD3-depleted haploidentical stem cell graft for paediatric refractory haematological malignancies

Br J Haematol. 2006 Nov;135(4):524-32. doi: 10.1111/j.1365-2141.2006.06330.x. Epub 2006 Sep 28.

Abstract

The main obstacles to successful haploidentical haematopoietic stem cell transplantation from a mismatched family member donor are delayed immune reconstitution, vulnerability to infections and severe graft-versus-host disease (GvHD). We designed a reduced-intensity conditioning regimen that excluded total body irradiation and anti-thymocyte globulin in order to expedite immune reconstitution after a CD3-depleted haploidentical stem cell transplant. This protocol was used to treat 22 paediatric patients with refractory haematological malignancies. After transplantation, 91% of the patients achieved full donor chimaerism. They also showed rapid recovery of CD3(+) T-cells, T-cell receptor (TCR) excision circle counts, TCRbeta repertoire diversity and natural killer (NK)-cells during the first 4 months post-transplantation, compared with those results from a group of patients treated with a myeloablative conditioning regimen. The incidence and extent of viremia were limited and no lethal infection was seen. Only 9% of patients had grade 3 acute GvHD, while 27% patients had grade 1 and another 27% had grade 2 acute GvHD. This well-tolerated regimen appears to accelerate immune recovery and shorten the duration of early post-transplant immunodeficiency, thereby reducing susceptibility to viral infections. Rapid T-cell reconstitution, retention of NK-cells in the graft and induction of low grade GvHD may also enhance the potential anti-cancer immune effect.

Publication types

  • Evaluation Study
  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • B-Lymphocytes / immunology
  • CD3 Complex / blood
  • Child
  • Child, Preschool
  • Female
  • Flow Cytometry
  • Graft Survival / immunology
  • Graft vs Host Disease / immunology
  • Hematologic Neoplasms / immunology
  • Hematologic Neoplasms / therapy*
  • Hematopoietic Stem Cell Transplantation / methods*
  • Humans
  • Killer Cells, Natural / immunology
  • Lymphocyte Count
  • Lymphocyte Depletion*
  • Male
  • Opportunistic Infections / immunology
  • Opportunistic Infections / prevention & control
  • Receptors, Antigen, T-Cell, alpha-beta / analysis
  • T-Lymphocyte Subsets / immunology
  • Transplantation Chimera / immunology
  • Transplantation Conditioning / methods*
  • Viral Load
  • Viremia / immunology
  • Viremia / prevention & control

Substances

  • CD3 Complex
  • Receptors, Antigen, T-Cell, alpha-beta